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Deciphering enhancers of hearing loss genes for efficient and targeted gene therapy of hereditary deafness 期刊论文
NEURON, 2025
作者:  Simeng Zhao
Adobe PDF(9318Kb)  |  收藏  |  浏览/下载:41/8  |  提交时间:2025/05/12
Lung-Specific mRNA Delivery by Ionizable Lipids with Defined Structure-Function Relationship and Unique Protein Corona Feature 期刊论文
ADVANCED SCIENCE, 2025
作者:  He, Xiaoyan;  Wang, Runyuan;  Cao, Yan;  Ding, Yan;  Chang, Yan
Adobe PDF(14333Kb)  |  收藏  |  浏览/下载:96/12  |  提交时间:2025/03/03
Histological Validation of Multi-Echo Gradient Echo (MGRE)-Derived Myelin Water Fraction (MWF) at 9.4 T and the Influence of Orientation on Quantification 期刊论文
NMR IN BIOMEDICINE, 2025, 卷号: 38, 期号: 1
作者:  Thompson, Garth John;  Wang, Ziyi;  Kim, Jae-Yoon;  Li, Hui;  Kim, Dong-Hyun
Adobe PDF(4180Kb)  |  收藏  |  浏览/下载:101/3  |  提交时间:2025/01/10
Targeted Delivery of mRNA with Polymer-Lipid Nanoparticles for In Vivo Base Editing 期刊论文
ACS NANO, 2025, 卷号: 19, 期号: 8
作者:  Chen, Qimingxing;  Chang, Yan;  He, Xiaoyan;  Ding, Yan;  Wang, Runyuan
Adobe PDF(12364Kb)  |  收藏  |  浏览/下载:145/26  |  提交时间:2025/02/28
A novel AAV Vector for gene therapy of RPE-related retinal degenerative diseases via intravitreal delivery 期刊论文
MOLECULAR NEURODEGENERATION, 2024, 卷号: 19, 期号: 1
作者:  Gong, Yajun;  Huang, Xianyu;  Tu, Tianxiang;  Chu, Cenfeng;  Xian, Chunrui
Adobe PDF(1205Kb)  |  收藏  |  浏览/下载:276/8  |  提交时间:2024/12/17
Impaired brain glucose metabolism in glucagon-like peptide-1 receptor knockout mice 期刊论文
NUTRITION & DIABETES, 2024, 卷号: 14, 期号: 1
作者:  Li, Hui;  Fang, Yujiao;  Wang, Da;  Shi, Bowen;  Thompson, Garth J.
Adobe PDF(1795Kb)  |  收藏  |  浏览/下载:256/5  |  提交时间:2024/11/04
Efficient expansion and CRISPR-Cas9-mediated gene correction of patient-derived hepatocytes for treatment of inherited liver diseases 期刊论文
CELL STEM CELL, 2024, 卷号: 31, 期号: 8
作者:  Zhang, Kun;  Wan, Ping;  Wang, Liren;  Wang, Zhen;  Tan, Fangzhi
Adobe PDF(9769Kb)  |  收藏  |  浏览/下载:378/10  |  提交时间:2024/08/26
AwakeRodent, the multi-center, multi-species, multi-modality study! 会议论文
INTERNATIONAL SOCIETY FOR MAGNETIC RESONANCE IN MEDICINE, 新加坡, 2024.5.4-2024.5.9
作者:  Marie E Galteau;  Binshi Bo;  Hui Li;  Mengchao Pei;  Mengyang Xu
Adobe PDF(483Kb)  |  收藏  |  浏览/下载:515/19  |  提交时间:2024/06/14
Critical role of TPRN rings in the stereocilia for hearing 期刊论文
MOLECULAR THERAPY, 2024, 卷号: 32, 期号: 1
作者:  Qi, Jieyu;  Tan, Fangzhi;  Zhang, Liyan;  Zhou, Yinyi;  Zhang, Ziyu
Adobe PDF(6596Kb)  |  收藏  |  浏览/下载:453/5  |  提交时间:2024/03/04
Differential Effect of Global Signal Regression Between Awake and Anesthetized Conditions in Mice 期刊论文
BRAIN CONNECTIVITY, 2024
作者:  Wang, Da;  Li, Hui;  Xu, Mengyang
Adobe PDF(3654Kb)  |  收藏  |  浏览/下载:431/5  |  提交时间:2024/03/04
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