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Targeted Delivery of mRNA with Polymer-Lipid Nanoparticles for In Vivo Base Editing 期刊论文
ACS NANO, 2025, 卷号: 19, 期号: 8, 页码: 7835-7850
作者:  Chen, Qimingxing;  Chang, Yan;  He, Xiaoyan;  Ding, Yan;  Wang, Runyuan
Adobe PDF(12364Kb)  |  收藏  |  浏览/下载:161/28  |  提交时间:2025/02/28
Engineered mitochondrial A-to-G editors with enhanced efficiency and targeting scope 预印本
2024
作者:  Chen, Liang;  Hong, Mengjia;  Luan, Changming;  Yuan, Meng;  Wang, Yiming
Adobe PDF(6044Kb)  |  收藏  |  浏览/下载:235/75  |  提交时间:2025/01/06
Engineered IscB-uRNA system with improved base editing efficiency for disease correction via single AAV delivery in mice 期刊论文
CELL REPORTS, 2024, 卷号: 43, 期号: 11, 页码: 114973
作者:  guo,ruochen;  sun,xiaozhi;  wang,feizuo;  han,dingyi;  yang,qiaoxia
Adobe PDF(7204Kb)  |  收藏  |  浏览/下载:233/7  |  提交时间:2024/12/02
Adenine base editor–mediated splicing remodeling activates noncanonical splice sites 期刊论文
JOURNAL OF BIOLOGICAL CHEMISTRY, 2023, 卷号: 299, 期号: 12
作者:  Liu, Yuanyuan;  Li, Qing;  Yan, Tong;  Chen, Haoran;  Wang, Jiahua
Adobe PDF(2791Kb)  |  收藏  |  浏览/下载:353/1  |  提交时间:2023/12/22
Progress and Prospects of Gene Editing in Pluripotent Stem Cells 期刊论文
BIOMEDICINES, 2023, 卷号: 11, 期号: 8
作者:  Zhang, Zhenwu;  Bao, Xinyu;  Lin, Chao-Po
Adobe PDF(1162Kb)  |  收藏  |  浏览/下载:1659/746  |  提交时间:2023/09/11
PE-STOP: A versatile tool for installing nonsense substitutions amenable for precise reversion 期刊论文
JOURNAL OF BIOLOGICAL CHEMISTRY, 2023, 卷号: 299, 期号: 8
作者:  Song, Ziguo;  Zhang, Guiquan;  Huang, Shuhong;  Liu, Yao;  Li, Guanglei
Adobe PDF(1357Kb)  |  收藏  |  浏览/下载:659/1  |  提交时间:2023/07/28
Advances in CRISPR/Cas gene therapy for inborn errors of immunity 期刊论文
FRONTIERS IN IMMUNOLOGY, 2023, 卷号: 14
作者:  Liu, Xinyi;  Li, Guanglei;  Liu, Yin;  Zhou, Fuling;  Huang, Xingxu
Adobe PDF(2489Kb)  |  收藏  |  浏览/下载:1327/319  |  提交时间:2023/05/05
PAM-Expanded Streptococcus thermophilus Cas9 C-to-T and C-to-G Base Editors for Programmable Base Editing in Mycobacteria 期刊论文
ENGINEERING, 2022
作者:  Zhang, Hongyuan;  Zhang, Yifei;  Wang, Wei-Xiao;  Chen, Weizhong;  Zhang, Xia
Adobe PDF(4002Kb)  |  收藏  |  浏览/下载:450/0  |  提交时间:2022/08/12
Correction of the pathogenic mutation in TGM1 gene by adenine base editing in mutant embryos 期刊论文
MOLECULAR THERAPY, 2022, 卷号: 30, 期号: 1
作者:  Dang, Lu;  Zhou, Xueliang;  Zhong, Xiufang;  Yu, Wenxia;  Huang, Shisheng
Adobe PDF(2575Kb)  |  收藏  |  浏览/下载:405/1  |  提交时间:2021/11/01
Developing PspCas13b-based enhanced RESCUE system, eRESCUE, with efficient RNA base editing 期刊论文
CELL COMMUNICATION AND SIGNALING, 2021, 卷号: 19, 期号: 1
作者:  Li, Guo;  Wang, Yihan;  Li, Xiangyang;  Wang, Yuzhe;  Huang, Xingxu
Adobe PDF(1212Kb)  |  收藏  |  浏览/下载:768/234  |  提交时间:2021/08/27
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