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Engineered IscB-WRNA system with improved base editing efficiency for disease correction via single AAV delivery in mice 期刊论文
CELL REPORTS, 2024, 卷号: 43, 期号: 11
作者:  Guo, Ruochen;  Sun, Xiaozhi;  Wang, Feizuo;  Han, Dingyi;  Yang, Qiaoxia
Adobe PDF(7204Kb)  |  收藏  |  浏览/下载:175/3  |  提交时间:2024/12/04
Engineered IscB-uRNA system with improved base editing efficiency for disease correction via single AAV delivery in mice 期刊论文
CELL REPORTS, 2024, 卷号: 43, 期号: 11, 页码: 114973
作者:  guo,ruochen;  sun,xiaozhi;  wang,feizuo;  han,dingyi;  yang,qiaoxia
Adobe PDF(7204Kb)  |  收藏  |  浏览/下载:216/6  |  提交时间:2024/12/02
Engineering a transposon-associated TnpB-Ï RNA system for efficient gene editing and phenotypic correction of a tyrosinaemia mouse model 期刊论文
NATURE COMMUNICATIONS, 2024, 卷号: 15, 期号: 1
作者:  Li, Zhifang;  Guo, Ruochen;  Sun, Xiaozhi
Adobe PDF(1961Kb)  |  收藏  |  浏览/下载:372/93  |  提交时间:2024/03/04
Engineering transposon-associated TnpB-1 ωRNA system for efficient gene editing and disease treatment in mouse 预印本
2023
作者:  Li, Zhifang;  Guo, Ruochen;  Sun, Xiaozhi;  Li, Guoling;  Liu, Yuanhua
Adobe PDF(6121Kb)  |  收藏  |  浏览/下载:196/0  |  提交时间:2024/01/09
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