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Expanding RNA editing toolkit using an IDR-based strategy 期刊论文
MOLECULAR THERAPY - NUCLEIC ACIDS, 2024, 卷号: 35, 期号: 2
作者:  Di MH(邸明慧);  Lv JJ(吕君君);  Jing ZY(荆征宇);  Yang YJ(杨艺杰);  Yan KL(闫昆仑)
Adobe PDF(3244Kb)  |  收藏  |  浏览/下载:413/10  |  提交时间:2024/04/28
Engineering Miniature CRISPR-Cas Un1Cas12f1 for Efficient Base Editing 期刊论文
MOLECULAR THERAPY: NUCLEIC ACIDS, 2024, 卷号: 35, 期号: 2
作者:  Hu, Yueer;  Han, Linxiao;  Mo, Qiqin;  Du, Zengming;  Jiang, Wei
Adobe PDF(3894Kb)  |  收藏  |  浏览/下载:350/7  |  提交时间:2024/05/10
A novel base editor SpRY-ABE8eF148A mediates efficient A-to-G base editing with a reduced off-target effect 期刊论文
MOLECULAR THERAPY - NUCLEIC ACIDS;, 2023, 卷号: 31, 页码: 78-87
作者:  Li, Guo;  Cheng, Yaxian;  Li, Yeqiu;  Ma, Hongru;  Pu, Zhongji
Adobe PDF(3134Kb)  |  收藏  |  浏览/下载:299/0  |  提交时间:2023/03/24
Engineering an adenine base editor in human embryonic stem cells with minimal DNA and RNA off-target activities 期刊论文
MOLECULAR THERAPY: NUCLEIC ACIDS, 2022, 卷号: 29
作者:  Zhang, Zhenwu;  Tao, Wanyu;  Huang, Shisheng;  Sun, Wenjun
Adobe PDF(1138Kb)  |  收藏  |  浏览/下载:420/6  |  提交时间:2022/09/16
Engineering of near-PAMless adenine base editor with enhanced editing activity and reduced off-target 期刊论文
MOLECULAR THERAPY-NUCLEIC ACIDS, 2022, 卷号: 28
作者:  Cao, Xiaofang;  Guo, Junfan;  Huang, Shisheng
Adobe PDF(3670Kb)  |  收藏  |  浏览/下载:278/3  |  提交时间:2022/09/13
CABE-RY: A PAM-flexible dual-mutation base editor for reliable modeling of multi-nucleotide variants 期刊论文
MOLECULAR THERAPY: NUCLEIC ACIDS, 2021, 卷号: 26
作者:  Tao, Wanyu;  Liu, Qing;  Huang, Shisheng;  Wang, Xin;  Qu, Shiyuan
Adobe PDF(3982Kb)  |  收藏  |  浏览/下载:448/6  |  提交时间:2021/09/29
Modeling a cataract disorder in mice with prime editing 期刊论文
MOLECULAR THERAPY-NUCLEIC ACIDS, 2021, 卷号: 25, 页码: 494-501
作者:  Lin, Jianxiang;  Liu, Xingchen;  Lu, Zongyang;  Huang, Shisheng;  Wu, Susu
Adobe PDF(1747Kb)  |  收藏  |  浏览/下载:274/0  |  提交时间:2021/11/25
Efficient Generation of Pathogenic A-to-G Mutations in Human Tripronuclear Embryos via ABE-Mediated Base Editing 期刊论文
MOLECULAR THERAPY-NUCLEIC ACIDS, 2019, 卷号: 17, 页码: 289-296
作者:  Li, Guanglei;  Liu, Xinyi;  Huang, Shisheng;  Zeng, Yanting;  Yang, Guang
Adobe PDF(1676Kb)  |  收藏  |  浏览/下载:863/264  |  提交时间:2019/10/28
Improving Editing Efficiency for the Sequences with NGH PAM Using xCas9-Derived Base Editors 期刊论文
MOLECULAR THERAPY-NUCLEIC ACIDS, 2019, 卷号: 17, 页码: 626-635
作者:  Liu, Xinyi;  Li, Guanglei;  Zhou, Xueliang;  Qiao, Yunbo;  Wang, Ruixuan
Adobe PDF(2762Kb)  |  收藏  |  浏览/下载:730/244  |  提交时间:2019/10/28
Deletion of miR-126a Promotes Hepatic Aging and Inflammation in a Mouse Model of Cholestasis 期刊论文
MOLECULAR THERAPY-NUCLEIC ACIDS, 2019, 卷号: 16, 页码: 494-504
作者:  Yan, Yi;  Qin, Dan;  Hu, Bian;  Zhang, Chunjing
Adobe PDF(3047Kb)  |  收藏  |  浏览/下载:489/3  |  提交时间:2019/07/01
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